Rare Disease, Cell & Gene Therapy Monthly RoundUp

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Welcome to P4A Let’s Talk Rare, a monthly podcast highlighting the most important developments in the world of rare diseases orphan drug, cell and gene therapy, hosted by Georgie Rack and Owen Bryant of Partners For Access. To find out more about Partners For Access and our commitment to sustainable orphan drug access for patients with high unmet need, visit partners4access.com

Recent Episodes
  • AI for Rare Disease: From Discovery to Trials, Smarter and Faster
    May 29, 2025 – 00:37:48
  • Improving Alignment In Drug Development
    Apr 28, 2025 – 00:36:35
  • Breaking Barriers
    Mar 31, 2025 – 00:27:44
  • P4A's 5 Top Trends for 2025
    Jan 31, 2025 – 00:27:22
  • The JCA is live
    Jan 13, 2025 – 00:25:24
  • Innovative Treatments for Cutaneous T-Cell Lymphoma with Leonard Mazur of Citius Pharmaceuticals
    Nov 19, 2024 – 00:26:21
  • Amplifying Patient Voices: Wes Michael on Rare Disease Advocacy
    Oct 10, 2024 – 00:23:54
  • Impact of Mergers, Acquisitions, and Patent Expirations on Job Cuts in Pharma and Biotech: Insights from Aurelija Luko and Darren Callanan
    Jul 2, 2024 – 00:27:15
  • The Role of Patient Experience Data in Drug Development with Pina Haberl and Sam Morrison
    May 3, 2024 – 00:34:37
  • World EPA Conference 2024 Special
    Apr 10, 2024 – 00:28:54
  • Rare Disease Day Special 2024: The Role of Genetic Diagnosis in Rare Conditions with Nick Meade
    Feb 29, 2024 – 00:24:31
  • Celebrating 5 Years of P4A: Reflections on Rare Diseases, Cell and Gene Therapies, and Legislation in Europe
    Jan 2, 2024 – 00:53:45
  • Revolutionizing Patient Outcomes: The Power of Digital Health Solutions with RJ Kedziora
    Dec 1, 2023 – 00:28:02
  • The Future of Patient Engagement and the Role of Technology in Healthcare with Iola Forster
    Oct 6, 2023 – 00:23:38
  • Navigating the New EU HTA Regulation and Its Impact on ATMP Development
    Jul 31, 2023 – 00:16:35
  • Alejandro Dorenbaum, CMO of Reneo Pharmaceuticals Discusses Clinical-Stage Therapies
    Jun 1, 2023 – 00:16:14
  • Interview with Xortx Therapeutics CEO, Dr Allen Davidoff discussing their journey from early development to potential launch
    Apr 29, 2023 – 00:19:22
  • World EPA Congress 2023 Special
    Apr 17, 2023 – 00:24:09
  • Rare Disease Day Special 2023
    Feb 28, 2023 – 00:40:03
  • Trends to look out for in 2023
    Feb 3, 2023 – 00:44:17
  • World Orphan Drug Congress Europe 2022 Special
    Dec 20, 2022 – 00:42:39
  • Winds of change for German Healthcare Market!
    Oct 31, 2022 – 00:38:42
  • Part 2 -Patient Empowerment: Is it a no-brainer?
    Oct 3, 2022 – 00:28:25
  • Part 1 Patient Empowerment; Why involving patients from early drug development through to launch is a no-brainer!
    Sep 13, 2022 – 00:31:08
  • What makes P4A an award winning consultancy?
    Jul 29, 2022 – 00:15:03
  • Special Episode with EUCOPE-Part 2 with Alexander Natz
    Jun 30, 2022 – 00:28:57
  • Special series with Eucope: Part 1 featuring Victor Maertens
    May 31, 2022 – 00:24:51
  • China market access: obstacle or opportunity for orphan drug, cell and gene therapy manufacturers?
    Apr 29, 2022 – 00:10:27
  • Should the Middle East be a priority launch market for orphan drug manufacturers?
    Mar 31, 2022 – 00:12:34
  • Rare Disease Day Special featuring Janet Bloor and Nick Meade - February 2022
    Feb 28, 2022 – 00:28:47
  • P4A Insights: Trends to look out for in 2022
    Feb 4, 2022 – 00:10:32
  • Special episode - Bluebird Bio: What went wrong? -December 2021:
    Dec 13, 2021 – 00:17:15
  • Special episode featuring James Mackay - November 2021
    Nov 30, 2021 – 00:23:59
  • Monthly Roundup - October 2021
    Oct 29, 2021 – 00:10:59
  • Monthly RoundUp - September 2021
    Sep 30, 2021 – 00:15:41
  • Monthly RoundUp: July 2021
    Jul 30, 2021 – 00:15:01
  • Monthly RoundUp - June 2021
    Jun 30, 2021 – 00:07:43
  • Monthly RoundUp - May 2021
    May 31, 2021 – 00:09:32
  • Monthly RoundUp - April 2021
    Apr 30, 2021 – 00:20:58
  • Monthly RoundUp - March 2021
    Mar 31, 2021 – 00:13:22
  • Monthly RoundUp - February 2021
    Feb 27, 2021 – 00:22:50
  • Rare Disease Day special episode: Reclaiming the rare disease patient’s voice
    Jan 29, 2021 – 00:36:55
  • End of year 2020 review
    Dec 21, 2020 – 00:18:03
  • Special episode: Gene Therapy access from a specialty pharmacy perspective
    Jun 22, 2020 – 00:20:50
  • Weekly RoundUp: February 29, 2020
    Feb 29, 2020 – 00:17:56
  • Weekly Roundup: December 30, 2019
    Dec 30, 2019 – 00:09:56
  • Weekly Roundup: December 23, 2019
    Dec 23, 2019 – 00:04:54
  • Weekly Roundup: November 12, 2019
    Nov 12, 2019 – 00:14:27
  • Weekly Roundup: November 5, 2019
    Nov 5, 2019 – 00:08:15
  • Weekly RoundUp: August 5, 2019
    Aug 5, 2019 – 00:18:35
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